CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular Therapy - Nucleic Acids

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CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
PDF) Establishing induced pluripotent stem cell lines from two
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
PDF) Modelling autosomal dominant optic atrophy associated with
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Characterisation of a novel OPA1 splice variant resulting in
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
PDF) Optimized OPA1 Isoforms 1 and 7 Provide Therapeutic Benefit
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
OPA1 Mutation and Late‐Onset Cardiomyopathy: Mitochondrial
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Enhanced genome editing in human iPSCs with CRISPR-CAS9 by co
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR-Cpf1 correction of muscular dystrophy mutations in human
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Frontiers Establishing induced pluripotent stem cell lines from
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
IJMS, Free Full-Text
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
OPA1 Mutation and Late‐Onset Cardiomyopathy: Mitochondrial
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Melatonin Repairs Osteoporotic Bone Defects in Iron-Overloaded
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Biomedicines, Free Full-Text
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
OPA1 regulation of mitochondrial dynamics in skeletal and cardiac
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
JCM, Free Full-Text
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