CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
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Molecular Therapy - Nucleic Acids, Vol 26, Pages 1-1480 (3 December 2021)
Oxidative stress monitoring in iPSC-derived motor neurons using genetically encoded biosensors of H2O2
Loss of OPA1 disturbs cellular calcium homeostasis and sensitizes for excitotoxicity
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular Therapy - Nucleic Acids
IJMS, Free Full-Text
CRISPRi gene modulation and all-optical electrophysiology in post-differentiated human iPSC-cardiomyocytes
Dead Cas(t) light on new life: CRISPRa-mediated reprogramming of somatic cells into neurons
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
IJMS, Free Full-Text
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